One child in 12,000 is born with Rett Syndrome - a genetic disorder that ... She took to her Instagram to share a slew of sweet photos of her teenage sister with her eldest son Kai, 15, who ...
Two UA Workshops to Celebrate International Day of Women and Girls in ScienceThe University of Alicante (UA), in ...
Background Rett syndrome is a complex genetic disorder with age-specific manifestations and over half of the patients surviving into middle age. However, little information about the phenotype of ...
Discover Stoke Therapeutics' innovative RNA-based treatments like zorevunersen for Dravet syndrome, with a promising pipeline ...
Taysha Gene Therapies' TSHA-102 tackles Rett syndrome’s root cause with its miniMECP2 transgene and scAAV delivery. So far, this is TSHA’s main value driver, and it appears safe and effective ...
Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...
Rare diseases have become an attractive target for pharmaceutical companies both in Australia and internationally with ...
Special Report: Neurotech International has inked a deal with a European leader in development and scale up of cannabis-based ...
It didn’t take long for Kennesaw State University student Lilianna Kocai to discover a passion for research. All it took was ...