To learn about the progress being made in the RNA therapeutics space, we spoke to CTO and Co-Founder of La Jolla Labs, Jeff ...

RNA-based medicines are one of the most promising ways to fight human disease, as demonstrated by the recent successes of RNA ...

Imagine a breakthrough in cancer treatment where only malignant cells are targeted, sparing healthy host cells; or patients with abnormal protein synthesis are treated to produce a healthy protein.

There are many molecules with therapeutic potential, but it can be a challenge to deliver them to the right places at the ...

UMD researchers have discovered key mechanisms in gene regulation that could improve the design of RNA-based medicines.

The CRISPR-Cas gene scissors offer a wide range of potential applications, from the treatment of genetic diseases to ...

Discover Stoke Therapeutics' innovative RNA-based treatments like zorevunersen for Dravet syndrome, with a promising pipeline ...

Analysis by Mount Sinai researcher from First-of-its kind global trial could lead to future therapies to prevent deadly ...

A new discovery offers hope for Huntington’s disease. This discovery provides hope that a DNA repair process may help slow or ...

Researchers uncover key mechanisms in gene regulation that may lead to better design of RNA-based medicines.