The goal of treatment for plexiform neurofibromas when they are diagnosed is to help that individual patient with how they're affecting them. So for many of those patients, those plexiform ...
Neurofibromatosis type 1 (NF1) is a rare genetic disorder that affects the nervous system, causing tumors to form on nerves ...
The approval was based on the findings from the ReNeu (NCT03962543) trial, which is the largest multicenter study of NF1 PN conducted to date. 2 Mirdametinib demonstrated a statistically ...