Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The ...

Robert Davidson is the first UK patient recruited to a new medical trial looking to support children with heart failure ...

Cumberland Pharmaceuticals Inc. (Nasdaq: CPIX), a specialty pharmaceutical company with development efforts focused on new products for rare diseases, today announced positive top-line results from ...

Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single Elevidys infusion.

Most people who carry the mutations develop symptoms of muscle weakness before age ... an investigational gene therapy for children with a type of limb-girdle muscular dystrophy called LGMD2C or ...

The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National Ambassador. Sander joins MDA National Ambassador Ira Walker from Fort ...

Symptoms of Muscular Dystrophy Congenital Muscular Dystrophy Congenital means ... Genetic diseases result from mutations to a parent’s gene that are then passed on to their child or children, causing ...

Get Instant Summarized Text (Gist) Muscular strength and cardiorespiratory fitness are significantly linked to a lower risk of death in cancer patients. A pooled analysis of 42 studies involving ...

RSV, or respiratory syncytial virus, usually causes mild symptoms akin to cold that go away on their own. But for babies, some young children and older adults, it can be serious. The flu spreads ...

The tiny tot was diagnosed with muscular dystrophy ... son’s symptoms wouldn’t fully manifest until he reached his teenage years. And when the mum read about life expectancy for children ...

The single mother of three claimed she left her two toddlers, ages 3 and 2, alone for a moment in early January so she could use the bathroom while prepping for a birthday party, People magazine ...