Discover Stoke Therapeutics' innovative RNA-based treatments like zorevunersen for Dravet syndrome, with a promising pipeline ...
The website restofworld got entries from 45 countries for a photo contest focusing on technology. Here are their top picks — ...
Special Report: Neurotech International has inked a deal with a European leader in development and scale up of cannabis-based ...
Rare diseases have become an attractive target for pharmaceutical companies both in Australia and internationally with ...
Background Rett syndrome is a complex genetic disorder with age-specific manifestations and over half of the patients surviving into middle age. However, little information about the phenotype of ...
Three of the patients had suffered post-traumatic visual discomfort especially when exposed to bright light, one experienced a phosphene in the central visual field and 23 patients complained of ...
Radiomics-Based Assessment of Primary Sjögren’s Syndrome From Salivary Gland Ultrasonography Images. IEEE J Biomed Health Inform. 2020 Mar;24(3):835-843. [2]Vukicevic AM, Radovic M, Zabotti A, Milic V ...
The company's first drug candidate trofinetide – marketed as DAYBUE – is approved by the FDA and Health Canada for the treatment of Rett syndrome. Neuren has granted an exclusive worldwide licence to ...
A selection of some of the most striking sports photographs taken around the world over the past seven days: Florian Schieder of Italy prepares at the start for the first Men's Downhill training ...
Taysha Gene Therapies' TSHA-102 tackles Rett syndrome’s root cause with its miniMECP2 transgene and scAAV delivery. So far, this is TSHA’s main value driver, and it appears safe and effective ...
Roula Khalaf, Editor of the FT, selects her favourite stories in this weekly newsletter. Hundreds of thousands of displaced Palestinians moved north on Monday after Israeli forces withdrew from ...
What is Zollinger-Ellison syndrome? Zollinger-Ellison syndrome (ZES) is a rare digestive disorder. If you have ZES, you likely have 1 or more tumors in the first part of the small intestine, the ...
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