A pair of clinical data sets gives Novartis confidence in a new formulation of the company’s gene therapy Zolgensma for the ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

One patient with Duchenne muscular dystrophy (DMD) has passed away following treatment with Sarepta Therapeutics’ gene therapy Elevidys, the biotech ...

The patient underwent treatment in December with Sarepta's therapy, called Elevidys, the company told Reuters in an emailed statement. Elevidys is the only FDA-approved gene therapy for Duchenne ...

Over time, this decrease would result in hepatic atrophy and a shrunken liver on imaging. The fully occlusive PVT would lead to proximal portal hypertension. The progressive hepatic atrophy could ...

Sarepta Therapeutics said early Tuesday that a patient had died after receiving its gene therapy Elevidys, which treats the rare genetic condition Duchenne muscular dystrophy. A young man with ...

Sarepta stock crashed Tuesday after a patient who received its approved gene therapy, Elevidys, died due to acute liver failure.

The two women accused of murder in the June 13 dehydration and starvation death of 3-year-old Sarai Perez-Rivera pleaded not ...

Health Canada is warning people that unauthorized sexual enhancement products sold in at least three provinces may pose serious health risks.

Shawn Kwatra, MD, FAAD, physician scientist at the University of Maryland Medical System, presented data at the American Academy of Dermatology 2025 annual conference on the rapid efficacy of topical ...

Smaller interlobular bile ducts may also show epithelial atrophy with severe cytological atypia. Furthermore, histological analysis of the liver parenchyma in patients with ischemic cholangitis ...