New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.
Our fundamental challenge is not simply to create the data. Rather, it is to collect and analyze it systematically. Doing so ...
According to research studies and demographic surveys by the Union Ministry of Tribal Affairs and genetic researchers, sickle cell disease is widespread in many tribal groups of India, especially amon ...
Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.
With the addition of Casgevy, Children’s Hospital Los Angeles now offers two gene therapies for sickle cell, the first being Lyfgenia.
NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...
Please provide your email address to receive an email when new articles are posted on . Sickle cell trait has no association with mortality from physical exertion or heat-related injuries without ...
A GROUNDBREAKING genetic treatment with the potential to cure sickle cell disease will be rolled out on the NHS. The one-off treatment costs more than £1million per patient but may essentially ...
A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...
Immvention Therapeutix is partnering with Novo Nordisk to develop oral treatments for sickle cell disease (SCD) and other ...
Sickle Cell Trait Does Not Cause "Sickle Cell Crisis" Leading to Exertion-Related Death: A Systematic Review. Blood Journal , 2025; DOI: 10.1182/blood.2024026899 Cite This Page : ...
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also known as exa-cel, was the first treatment to be licensed using gene ...